• 
  Acceleron Pharma: www.acceleronpharma.com
•  Akashi Therapeutics: www.akashirx.com
•  Armgo Pharma: www.armgo.com
• 
  Asklepios Biopharmaceutical: www.askbio.com
•  Astrazeneca: www.astrazeneca.com

•    Atlantic Gene Therapies: www.atlantic-gene-therapies.fr
•    Audentes Therapeutics: www.audentestx.com

•  Bamboo Therapeutics:  www.bambootherapeutics.com
•   Biomarin: www.bmrn.com
•  Bristol-Myers Squibb: www.bms.es
• 
  Cardoz AB: www.cardoz.com

• Capricor Therapeutics: www.capricor.com

• 
  Catabasis: www.catabasispharma.com
•  Cardero Therapeutics: www.carderox.com

Cellectis: www.cellectis.com

Crispr Therapeutics: www.crisprtx.com

                     Daiichi Sankyo: www.daiichi-sankyo.es

• Dart Therapeutics: www.dartrx.com
•   Eloxx Pharmaceuticals: www.eloxxpharma.com
•   EspeRare Foundation: esperare.org
•  Exonics Therapeutics: www.exonicstx.com
•   Eli Lilly and Company: www.lilly.com
•  Fate Therapeutics: www.fatetherapeutics.com
•   FibroGen: www.fibrogen.com
• 
  Galapagos: www.glpg.com
•   Genethon: www.genethon.fr
• 
  Glaxo Smith Kline (GSK): www.gsk.es www.gsk.com
• GTX: www.gtxinc.com
• 
  Halo Therapeutics: www.halotherapeutics.com

• 
  Ipsen: www.ipsen.com
•  Idera Pharmaceuticals: www.iderapharma.com

•   Italfármaco:  www.itfsp.com
• 
  Kaken pharmaceutical: www.kaken.co.jp/english/index.html
•  Mallinckrodt Pharmaceuticals: www.mallinckrodt.com
• Marathon Pharmaceuticals: www.marathonpharma.com
•  Milo Biotechnology: www.milobiotechnology.com
•    Mitobridge: www.mitobridge.com
• 
  N-Gen: www.ngene.us
•  Nicox: www.nicox.com
•    Nippon Shinyaku: www.nippon-shinyaku.co.jp
• Nobelpharma: www.nobelpharma.co.jp
• 
  Novartis: www.novartis.com
•  Pfizer: www.pfizer.com
• 
  Phrixus: www.phrixuspharmaceuticals.com
• 
  Prosensa: www.prosensa.eu
•   Prothelia:  www.prothelia.com
• 
  PTC Therapeutics: www.ptcbio.com
•   RASRx: www.rasrx.com
• 
  Retrophin: www.retrophin.com
• 
  Reveragen: www.reveragen.com
• 
  Santhera Pharmaceuticals: www.santhera.com
• 
  Sarepta Therapeutics: www.sareptatherapeutics.com
• 
  Shire: www.shire.com y www.shireiberica.com
•   Solid Biosciences: www.solidbio.com
• Som Biotech: www.sombiotech.com

• 
  Summit: www.summitplc.com
•  Synthena: www.synthena.com
•  Taiho Pharma: www.taiho.co.jp
•   Tarix Orphan:  www.tarixorphan.com
• 
  Tivorsan: www.tivorsan.com
•  Tonus Therapeutics: www.tonustherapeutics.com
•   Wabe Life Sciencies:  www.wavelifesciences.com