Acceleron Pharma: www.acceleronpharma.com
Akashi Therapeutics: www.akashirx.com
Armgo Pharma: www.armgo.com
Asklepios Biopharmaceutical: www.askbio.com
Astrazeneca: www.astrazeneca.com
Atlantic Gene Therapies: www.atlantic-gene-therapies.fr
Audentes Therapeutics: www.audentestx.com
Bamboo Therapeutics: www.bambootherapeutics.com
Biomarin: www.bmrn.com
Bristol-Myers Squibb: www.bms.es
Cardoz AB: www.cardoz.com
Capricor Therapeutics: www.capricor.com
Catabasis: www.catabasispharma.com
Cardero Therapeutics: www.carderox.com
Cellectis: www.cellectis.com
Crispr Therapeutics: www.crisprtx.com
Daiichi Sankyo: www.daiichi-sankyo.es
Dart Therapeutics: www.dartrx.com
Eloxx Pharmaceuticals: www.eloxxpharma.com
EspeRare Foundation: esperare.org
Exonics Therapeutics: www.exonicstx.com
Eli Lilly and Company: www.lilly.com
Fate Therapeutics: www.fatetherapeutics.com
FibroGen: www.fibrogen.com
Galapagos: www.glpg.com
Genethon: www.genethon.fr
Glaxo Smith Kline (GSK): www.gsk.es www.gsk.com
GTX: www.gtxinc.com
Halo Therapeutics: www.halotherapeutics.com
Ipsen: www.ipsen.com
Idera Pharmaceuticals: www.iderapharma.com
Italfármaco: www.itfsp.com
Kaken pharmaceutical: www.kaken.co.jp/english/index.html
Mallinckrodt Pharmaceuticals: www.mallinckrodt.com
Marathon Pharmaceuticals: www.marathonpharma.com
Milo Biotechnology: www.milobiotechnology.com-
Mitobridge: www.mitobridge.com 
N-Gen: www.ngene.us
Nicox: www.nicox.com
Nippon Shinyaku: www.nippon-shinyaku.co.jp
Nobelpharma: www.nobelpharma.co.jp
Novartis: www.novartis.com
Pfizer: www.pfizer.com
Phrixus: www.phrixuspharmaceuticals.com
Prosensa: www.prosensa.eu
Prothelia: www.prothelia.com
PTC Therapeutics: www.ptcbio.com
RASRx: www.rasrx.com
Retrophin: www.retrophin.com
Reveragen: www.reveragen.com
Santhera Pharmaceuticals: www.santhera.com
Sarepta Therapeutics: www.sareptatherapeutics.com
Shire: www.shire.com y www.shireiberica.com
Solid Biosciences: www.solidbio.com
Som Biotech: www.sombiotech.com
Summit: www.summitplc.com
Synthena: www.synthena.com
Taiho Pharma: www.taiho.co.jp
Tarix Orphan: www.tarixorphan.com
Tivorsan: www.tivorsan.com
Tonus Therapeutics: www.tonustherapeutics.com
Wabe Life Sciencies: www.wavelifesciences.com
